Rare Disease
We support scientific initiatives to aid in the development of genetic medicines for neglected rare diseases
Ultrarare diseases are often neglected by the pharmaceutical industry owing to the small number of patients who live with these conditions. The Research arm of the RTW Foundation contributes to addressing this problem in two ways: by providing advisory services to disease foundations interested in developing therapies for their patients, and by funding drug-discovery projects on ultrarare diseases.
Advisory services to disease foundations
We put our operational capabilities and our drug-discovery expertise to the service of the ultrarare disease community. Whether you have just created a new disease foundation or are already developing a therapeutic asset, we would be happy to provide our unbiased, expert opinion on the best path forward for your project. Get in touch for more information.
Funding for drug-discovery projects on ultrarare diseases
Our current funding priority focuses on drug-discovery projects on diseases that affect fewer than 1000 people worldwide and for which no commercial drug-development program exists. RTW Foundation aims to fund proposals co-developed by rare disease foundations and the Rare Disease Advisors that meaningfully accelerate research in a rare disease. Grant cycles take place in January, May, and September. We offer 3 types of grants for rare disease foundations. Find out how your foundation could be eligible for these grants.